Global pompe disease treatment market is rising gradually with a substantial CAGR of 8.81% in the forecast period of 2019-2026.. Special regulatory grants and drug designations for orphan drugs mainly for the treatment of the rare diseases such as Pompe disease are driving the market growth.
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An introduction of Pompe Disease Treatment Market 2019
Pompe disease is a genetic disorder that is caused by the buildup of a complex sugar called glycogen in cells and tissues. This accumulation of glycogen causes impairment in organs and tissues. This disease majorly causes muscle wasting, muscle weakness and other complications such as cardiac problems and respiratory disorders. GAA gene is responsible for breakdown of glycogen in the body. In Pompe disease, mutation occurs in GAA gene that results in accumulation of glycogen in tissues and organs.
The incidence rate of Pompe disease is approximately 1 in 40,000 births in the United States. Pompe disease occurs in males and females in same number. However, the incidence of this disease varies in different ethnic groups.
Topmost Outstanding Market Players are Amicus Therapeutics, Inc., Takeda Pharmaceutical Company, Sanofi,, Valerion Therapeutics, Sangamo Therapeutics, Oxyrane, EpiVax, Inc., Alexion Pharmaceuticals, Inc., Novartis AG, GlaxoSmithKline plc., Audentes Therapeutics, Spark Therapeutics, Inc., Pfizer Inc., BioMarin, ABIOMED, Sarepta Therapeutics,. Biogen, Genentech, Inc., among others.
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What are the Recent Development of the Market?
In February 2019 Amicus Therapeutics, Inc. received Breakthrough Therapy Designation from the U. S. FDA for AT-GAA a novel treatment that consist ATB200, a recombinant human acid alpha-glucosidase (rhGAA) enzyme used for the treatment of patients with Pompe disease. This grant will expedite the development and review of AT-GAA for pompe disease
In March 2017, Valerion Therapeutics developed VAL-1221, a combination fusion protein synthesized by antibody delivery technology and recombinant human acid alpha-glucosidase (rhGAA) for treatment of patients with Pompe disease. This therapy is advanced as it has the ability to act on glycogen present in cytoplasm of late-onset pompe disease patients. This development will bring an effective novel therapy for Pompe disease and enhance the market of the company
Worldwide Pompe Disease Treatment Industry 2019 Market Research Report is spread crosswise over 129 pages and gives restrictive essential insights, information, data, patterns and aggressive scene points of interest in this specialty division.
Global pompe disease treatment market is highly fragmented and the major players have used various strategies such as new product launches, expansions, agreements, joint ventures, partnerships, acquisitions, and others to increase their footprints in this market. The report includes market shares of Pompe disease treatment market for Global, Europe, North America, Asia-Pacific, South America and Middle East & Africa.
Crucial Market Segment details-:
- By Type (Classic Infantile-Onset Pompe Disease, Non-Classic Infantile-Onset Pompe Disease, Late-Onset Pompe Disease),
- Therapy Type (Medication, Enzyme Replacement Therapy, Physiotherapy, Others),
- Route of Administration (Oral, Injectable, Others),
- End Users (Hospitals, Homecare, Specialty Clinics, Others),
- Distribution Channel (Hospital Pharmacy, Online Pharmacy, Retail Pharmacy, Others)
Strategic Points Covered in Table of Content of Pompe Disease Treatment Market:
Chapter 1: Introduction, Definition, Specifications, Classification and Scope the Pompe Disease Treatment market 2019
Chapter 2: Exclusive Summery like Industry chain structure, Manufacturer cost structure, suppliers, etc
Chapter 3: Displays Trends, Drivers and Challenges of the Pompe Disease Treatment market
Chapter 4: By the study of SWOT analysis it displays sales analysis, investment analysis, market analysis, etc
Chapter 5: It evaluates the market by segments, by countries and by manufacturers with revenue, share and sales by key countries in these various regions.
Chapter 6: Evaluate the leading manufacturers of the Global Pompe Disease Treatment market which consists of its Competitive Landscape, Peer Group Analysis, BCG Matrix & Company Profile
Chapter 7: Pompe Disease Treatment Research Findings and Conclusion, Appendix, system and information source
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